Finding a Cure
Pierce is Partnering with:
“Together we can do great things”
- Mother Teresa
What is TECPR2?
TECPR2 is a progressive, neurodegenerative disease; it gets worse with time and attacks central nervous system. It is effectively Pediatric ALS. In time, it will take away a child’s ability to walk, talk, swallow and, ultimately, breathe.
What are symptoms?
Developmental delays, intellectual disability, speech and language delays, chronic respiratory infections, physical and motor function delays, various issues associated with the nervous system, the list goes on…
Is it Fatal?
Unfortunately, yes.
The oldest known child lived to just 19 years old.
Is there a treatment or cure?
Not yet, but where there is a will there is a way. Some incredibly smart, passionate, caring individuals have been working tirelessly to create one.
Together, we will cure TECPR2!
What’s been accomplished thus far?
The Eleanor Kaplan Foundation has been busy championing a cure since 2018 and has already assembled an incredible team!
Through collaborative efforts, incredible strides have been made toward doing the impossible and creating a successful Gene Therapy Cure for an Orphan Pediatric Disease.
Unprecedented levels of partnerships formed for an Orphan Pediatric Disease
What’s Gene Therapy?
What’s the team’s current progress?
Since 2022, this team which we are fortunate to now be part of, has developed a gene therapy proof of concept and successfully “infected” model mice with TECPR2.
And then cured them!!
There is now a process to remove the TECPR2 gene, replace it with a healthy one, and allow these kids to live.
We are successfully past the safety trials in mice and standing at the front door of manufacturing for human clinical trials.
Full Rescue in the Brain!
We are now gearing up for
Clinical Trials!
What’s next?
With enough fundraising, in just 2 years time, we can cure the entire population of children suffering from TECPR2. And that blueprint is just the beginning for what other genetic diseases we can cure.
How can I help?
Your love, support, thoughts, prayers, and well-wishes are the fuel that makes Pierce Fierce!! Your generosity can help cure TECPR2 and spreading his mission will help the fight against Pediatric Orphan Disease!